
Dedicated to developing
life-changing medicines
for patients and families living with challenging diseases

Dedicated to developing
life-changing medicines
for patients and families living with challenging diseases


Driven by the desire
to deliver meaningful therapeutic options
for patients in need


Driven by the desire to deliver better therapeutic options for patients in need


Driven by the desire to deliver better therapeutic options for patients in need
Virtual Investor: Alzheimer’s Disease Spotlight
Virtual Investor: Niemann-Pick Disease Type C Spotlight

