• Internationally recognized scientist, microbiologist and founder of CosmosID, a privately held bioinformatics firm
• Distinguished University Professor at U. Maryland and Johns Hopkins University
• Former Director, National Science Foundation (1998 – 2006)
• National Medal of Science awardee
• Member, US National Academy of Sciences

• Neuroscientist with more than 25 years’ experience in global health arena, public and private sectors
• Senior executive at NIH
• First president of non-profit Global Virus Network
• Former Member of President’s Council of Advisors on Science and Technology

Global Principal Investigator for Ongoing TransportNPC™ Study

• Pediatric hematologist oncologist, Director of Neuro-oncology, and Professor of Pediatrics, UCSF Benioff Children’s Hospital Oakland
• First physician in US to use cyclodextrins for treatment in NPC, compassionate use
• Advisor to US and Australian NPC Advocacy organizations and to physicians globally on NPC

• Over 15 years in senior leadership at Sanofi Genzyme, including Vice President of Rare Disease Clinical Development
• Led the clinical development of CRISPR-based genome editing medicines to treat human diseases, including the first approved IND for a CRISPR-based medicine to be delivered in vivo that is designed to treat a genetic form of blindness called Leber congenital amaurosis type 10.
• Affiliated with Boston Children’s Hospital during his entire career, where he is a part-time Staff Physician in Genetics; and is an Instructor in Pediatrics at Harvard Medical School.

• Gastroenterologist at Alameda Health System, CA and Highland Hospital
• Globally recognized expert in lipid metabolism
• First to discover that cyclodextrins release cholesterol from cells using an animal model
• Assistant Clinical Professor, UCSF